Sarepta reports a second death case related to its gene therapy

Zhitong
2025.06.15 13:56

Sarepta Therapeutics announced that another patient receiving its gene therapy for rare muscle diseases has died from acute liver failure. The company stated that this death occurred in a patient who received the one-time treatment drug Elevidys, and three months ago, a teenage boy died after receiving the treatment. Both cases involved patients with Duchenne muscular dystrophy who were unable to walk. The company has suspended a clinical trial, stopped shipping the drug to patients who cannot walk, and is considering strengthening the immunosuppressive regimen for these patients