Sarepta reports a second death case related to its gene therapy
Sarepta Therapeutics announced that another patient receiving its gene therapy for rare muscle diseases has died from acute liver failure. The company stated that this death occurred in a patient who received the one-time treatment drug Elevidys, and three months ago, a teenage boy died after receiving the treatment. Both cases involved patients with Duchenne muscular dystrophy who were unable to walk. The company has suspended a clinical trial, stopped shipping the drug to patients who cannot walk, and is considering strengthening the immunosuppressive regimen for these patients